Learn more about our global Phase 3 HARBOR™ study for DM1 and our positive long-term MARINA-OLE™ data including vHOT (a measurement of myotonia) video and patient testimonials

Targeting Therapeutic Oligonucleotides

The New England Journal of Medicine
Levin, AA. N Engl J Med 2017;376:1DOI 10.1056/NEJMcibr1613559